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Dernières publications
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Valentina Taglietti, Kaouthar Kefi, Lea Rivera, Oriane Bergiers, Nastasia Cardone, et al.. Thyroid-stimulating hormone receptor signaling restores skeletal muscle stem cell regeneration in rats with muscular dystrophy. Science Translational Medicine, 2023, 15 (685), ⟨10.1126/scitranslmed.add5275⟩. ⟨hal-04150315⟩
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A. Morin, Amalia Stantzou, Olga N. Petrova, John C.W. Hildyard, T. Tensorer, et al.. Dystrophin myonuclear domain restoration governs treatment efficacy in dystrophic muscle. Proceedings of the National Academy of Sciences of the United States of America, 2023, 120 (2), ⟨10.1073/pnas.2206324120⟩. ⟨hal-04122777⟩
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Valentina Taglietti, Kaouthar Kefi, Iwona Bronisz-Budzyńska, Busra Mirciloglu, Mathilde Rodrigues, et al.. Duchenne muscular dystrophy trajectory in R-DMDdel52 preclinical rat model identifies COMP as biomarker of fibrosis. Acta Neuropathologica Communications, 2022, 10 (1), ⟨10.1186/s40478-022-01355-2⟩. ⟨hal-03828280⟩
Chiffres clés
48
Publications avec texte intégral
Open Access
67 %
Mots clés
Dynamin 2
Delivery
Multiresolution modeling
Muscular dystrophy
Hear
Centronuclear myopathy
NAD+
LncRNA
Muscle Strength
Dystrophy
Homeostasis
Becker muscular dystrophy BMD
Gene modifiers
Epigenetics
Mitochondrial fission
Becker muscular dystrophy
Ex-vivo
Cell Biology
Becker muscular dystrophy BMD Duchenne muscular dystrophy DMD miRNA nNOS
Drp1
Multi exon skipping
Clinical trials
DMO
Human Umbilical Vein Endothelial Cells
Genomic
CaV subunits
Multi resolution modeling
Muscle development
Mdx mouse
Myogenesis
Autophagy
Metabolism
Duchenne DMD dystrophy
Male
MES
Skeletal muscle
Inhibitors
Muscle
Cardiomyopathy
Muscular Dystrophy
Cells
Inbred mdx
Dystrophie Musculaire de Becker BMD
Antisense oligonucleotides
DMD
Hepatocellular carcinoma
Molecular docking
Humans
Long QT
Myotendinous junction
Becker BMD muscular dystrophy
Liver
Duchenne muscular dystrophy
CTNNB1
Energy Metabolism/drug effects
CD38
L-Type
BMD
Mice
Exon skipping
NNOS
DHPR α1S
Dystrophine
Morphogenesis
Muscular Atrophy
Animal/physiopathology
Cell Line
Inbred C57BL
Calcium
Génomique
Cardiomyopathie
Cell homeostasis
MiARN
Animals
Dystrophie Musculaire de Duchenne DMD
Gene Expression Regulation/drug effects
CaVβs
Long noncoding RNA
Base Sequence
Diseases
Dystrophin-EGFP
Cultured
LKB1
Calcium Channels
Muscles/physiopathology
Gene expression
Dystrophin
Duchenne muscular dystrophy DMD
Allele‐specific silencing therapy
Modificateurs de gènes
Muscle Biology
Molecular Sequence Data
Dystrophin central domain
Invivo
Dystrophie musculaire de Becker
LncARN
Activin Receptors
Cachexia
Immunoglobulin Fc Fragments/pharmacology
Knockout